EU regulator says treatment could fill major gap for patients who lack a suitable stem cell donor and leads to sharp drops in severe infections and bleeding episodes.
Medscape News Europe
Source link : https://www.medscape.com/viewarticle/chmp-backs-first-gene-therapy-wiskott-aldrich-syndrome-2025a1000vqr?src=rss
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Publish date : 2025-11-14 14:02:00
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