FDA Approves First Drug for Rare Lipid Storage Disorder

(MedPage Today) — The FDA on Friday approved chenodiol (Ctexli) for the treatment of cerebrotendinous xanthomatosis (CTX) in adults.
Chenodiol — a naturally occurring human bile acid also known as chenodeoxycholic acid — is the first FDA…

Source link : https://www.medpagetoday.com/publichealthpolicy/fdageneral/114332

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Publish date : 2025-02-21 22:02:53

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