FDA Extends Approval of PKU Drug to Include Adolescents



Previously only approved for adults, BioMarin’s pegvaliase-pqpz (PALYNZIQ) is now licensed for patients as young as 12 years.
Medscape Medical News



Source link : https://www.medscape.com/viewarticle/fda-extends-approval-pku-drug-include-adolescents-2026a10006y2?src=rss

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Publish date : 2026-03-06 11:44:00

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