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FDA OKs SMA Gene Therapy Itvisma

November 25, 2025
in Health News
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Itvisma contains the active ingredient in Zolgensma approved in 2019 for children younger than 2 years but is reformulated for intrathecal administration across age groups.
Medscape Medical News



Source link : https://www.medscape.com/viewarticle/fda-oks-new-formulation-sma-gene-therapy-itvisma-2025a1000wyv?src=rss

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Publish date : 2025-11-25 16:41:00

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