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Gene Therapy Tops Nusinersen in Spinal Muscular Atrophy

October 16, 2025
in Health News
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Gene therapy is linked to better nonmotor outcomes in spinal muscular atrophy type 1 compared to first-line nusinersen, new data suggest.
Medscape Medical News



Source link : https://www.medscape.com/viewarticle/gene-therapy-tops-nusinersen-spinal-muscular-atrophy-2025a1000rw8?src=rss

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Publish date : 2025-10-16 08:08:00

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