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Gene Therapy Wins FDA Approval for Life-Threatening Immunodeficiency

December 10, 2025
in Health News
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(MedPage Today) — The FDA on Tuesday approved etuvetidigene autotemcel (Waskyra) as the first cell-based gene therapy for patients 6 months and older with Wiskott-Aldrich syndrome, a rare primary immunodeficiency.
The life-threatening genetic…



Source link : https://www.medpagetoday.com/genetics/generalgenetics/118940

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Publish date : 2025-12-10 21:39:00

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